WO2025003513 - OTOFERLIN GENE TRANSFER

National phase entry is expected:
Publication Number WO/2025/003513
Publication Date 02.01.2025
International Application No. PCT/EP2024/068451
International Filing Date 01.07.2024
Title **
[English] OTOFERLIN GENE TRANSFER
[French] TRANSFERT DE GÈNE D'OTOFERLINE
Applicants **
KATHOLIEKE UNIVERSITEIT LEUVEN KU Leuven Research & Development Waaistraat 6 - Box 5105 3000 Leuven, BE
Inventors
DE VIN, Filip c/o KULeuven R&D Waaistraat 6 - box 5105 3000 Leuven, BE
HENCKAERTS, Els c/o KULeuven R&D Waaistraat 6 - box 5105 3000 Leuven, BE
Priority Data
23182462.4   29.06.2023   EP
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Quotation for National Phase entry

Country StagesTotal
China Filing1021
EPO Filing, Examination4736
Japan Filing587
South Korea Filing574
USA Filing, Examination2710
MasterCard Visa

Total: 9628

The term for entry into the National Phase has expired. This quotation is for informational purposes only

Abstract[English] The invention relates to a first fusion protein comprising N-terminally an N-terminal fragment of otoferlin and C-terminally an N-terminal fragment of an intein, and a second fusion protein comprising N-terminally a C-terminal fragment of an intein and C-terminally a C-terminal fragment of intein.[French] L'invention concerne une première protéine de fusion comprenant N-terminalement un fragment N-terminal d'otoferline et C-terminalement un fragment N-terminal d'une intéine, et une seconde protéine de fusion comprenant N-terminalement un fragment C-terminal d'une intéine et C-terminalement un fragment C-terminal d'intéine.
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